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Revolutionizing Rare Disease Research: Unleashing the Power of Patient Advocacy and Artificial Intelligence

PM360

Despite the unique traits exhibited by approximately 11,000 rare diseases (RD), patients commonly face challenges due to the diseases’ low prevalence, including feelings of isolation and navigating overwhelming information about their condition 1. Another impeding factor in RD clinical trials is patient recruitment and ethnic diversity.

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Avrobio receives FDA rare pediatric disease status for cystinosis therapy

Pharmaceutical Technology

Avrobio has received rare pediatric disease designation from the US Food and Drug Administration (FDA) for its investigational gene therapy, AVR-RD-04, designed to treat cystinosis. AVR-RD-04 works by genetically modify a patient's hematopoietic stem cells (HSCs) to express the gene that encodes the cystinosin protein.

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Anthem Biosciences Pvt. Ltd-Walk-In Interview for ARD/ QC On 25th Feb’ 2023

Pharma Pathway

in Pharmaceutical analysis Experience: 1-6 years Location: Bommasandra/ Harohalli Date : 25th Feb’ 2023 Time: 09:00 AM to 12:00 PM Venue: No 49, Canara Bank Road, Hosur Rd, Electronics City Phase 1, Bommasandra Industrial Area, Bengaluru, Karnataka 560099 Anthem Biosciences Pvt.

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Alkem Laboratories Ltd -Walk-In Interviews for Engineering/ Manufacturing/ Technical Services On 5th March 2023

Pharma Pathway

902, 903, NAC Rd, Housing Board Chowk, Sector 13, Chandigarh, 160101 Contact: 01795-668999/ Bablesh.kumar@alkem.com Documents Required: Copy of your resume, Salary breakup/ Increment letter, Passport Size Photograph, Copy of Aadhaar & Pan Card. Date: 5th March 2023 Time: 09:30 AM to 04:00 PM Venue: Hotel Solitaire, SCO No.

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Avrobio receives orphan drug designation for Hunter syndrome gene therapy

Pharmaceutical Technology

Avrobio has received orphan drug designation for its gene therapy, AVR-RD-05, from the US Food and Drug Administration (FDA) to treat mucopolysaccharidosis type II (MPSII) or Hunter syndrome. AVR-RD-05 had previously obtained rare pediatric disease designation from the FDA.

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Teva Pharmaceuticals-Walk -In Interview for Multiple Positions On 24th Feb’ 2023

Pharma Pathway

37 & 37, Cts, 1, Bund Garden Rd, Next to Jehangir Hospital, Central Excise Colony, Sangamvadi, Pune, Maharashtra 411001 Teva Pharmaceuticals-Walk -In Interview for Multiple Positions On 24th Feb’ 2023

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Cipla Limited – Walk-In Drive for Diploma Chemical/ B.Tech Chemical/ B.Sc Chemistry On 26th Feb’ 2023

Pharma Pathway

Walk-In Drive for Diploma Chemical/ B.Tech Chemical/ B.Sc Chemistry On 26th Feb’ 2023 @ Cipla Limited Job Role: Production Operator/ Officer Designation: Senior Executive Qualification: Diploma Chemical/ B.Tech Chemical/ B.Sc Chemistry On 26th Feb’ 2023