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Novartis secures first-of-a-kind haematology approval

European Pharmaceutical Review

Therefore, with data showing that iptacopan is an “efficacious oral treatment with a demonstrated safety profile [this] could be practice-changing for physicians and help relieve burdens experienced by people with PNH,” Dr Pullarkat added. Patients avoiding transfusion: The transfusion avoidance rate was 95.2 percent for anti-C5.

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PhRMA lies to protect pharma profits

World of DTC Marketing

Meanwhile, the top 25 pharmaceutical companies reported a “healthy average operating margin of 22 percent” at the end of 2017, according to an analysis by GlobalData. About 40 percent of drugs fail in preliminary Phase I studies, which assess a drug’s safety in humans and typically cost just $25 million.

Pharma 255
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Collaboration with Janssen and Eli Lilly to address lack of paediatric medications

Pharmaceutical Technology

In recent years, with the advent of biologics and novel therapeutic targets such as anti-TNF, anti-interleukin, and anti-integrin, there has been a steady increase in the number of agents approved to treat inflammatory bowel diseases (IBD), which has provided physicians with an increasing number of options to treat Crohn’s disease (CD).

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Healthcare Watch September 2022

PM360

based physicians reveals that a majority are concerned and confused about what constitutes a life-threatening emergency that would make an abortion procedure legal in those 11 states where it has been banned. Doctor Docs: Doctors Left Concerned After Roe v. Wade Overturn. A recent Sermo study of 240 U.S.-based Or must it be 100%?”.

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Relief for Amylyx as FDA clears controversial ALS drug Relyvrio

pharmaphorum

The approval makes Relyvrio (sodium phenylbutyrate and taurursodiol) the first new therapy option for ALS – also known as motor neuron disease (MND) – since Mitsubishi Tanabe Pharma’s intravenous Radicava (edaravone) was cleared by the FDA in 2017. An oral version of edaravone was cleared this year.

FDA 87
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The Caregiver Vertical: How Pharma Engages

Pharma Marketing Network

Members of a multidisciplinary care team may include physicians, nurses, pharmacists, radiologists, dieticians…the list goes on. Caregiver observations of the patient experience over the progression of the disease may inform the safety and efficacy of a particular therapeutic. Connect at linkedin.com/in/sunnywhite/ . February 2019.

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Patient centricity and the changing pharmaceutical vista

pharmaphorum

Developing medicines – for people living with disease Dr Mullen’s current role involves providing medical monitoring support, as well as safety, pharmacovigilance, scientific, and medical advice across a range of client projects, including advanced therapies and orphan drugs.