Remove tag gene-therapy-analytical-development
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Pioneering the Path Pre- and Post-Launch Strategies

PM360

In the rapidly evolving landscape of healthcare, where breakthrough therapies and treatments emerge at an unprecedented pace, conventional boundaries are rapidly shifting. Post-launch, the role of Medical Affairs groups continues to evolve, focusing on driving patient outcomes and optimizing the use of therapies in real-world settings.

Medical 52
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Realising milestones with gene therapy for SMA

European Pharmaceutical Review

Novartis shared long-term data for its SMA gene therapy in March 2023, which indicated significant long-term motor-milestone achievements in spinal muscular atrophy (SMA). 3 The one-time gene therapy received final draft guidance from the National Institute for Health and Care Excellence (NICE) on 16 March 2023.