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Understanding a rare disease through the lens of real world and prevalence data

Clarivate

Degeneration of the retinal ganglion cells causes rapidly progressing vision loss, leading to permanent (non-painful) blindness within a year. “A Hospital-Based Five-Year Prospective Study on the Prevalence of Leber’s Hereditary Optic Neuropathy with Genetic Confirmation.” References [1] Sundaramurthy S et al.